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targeted treatments

Coverage of targeted treatments in the Nexus archive.

Earliest in view: Jul 31 · 08:30 UTCMost recent: Jul 31 · 08:30 UTC
Co-mentioned in this coverage
limb girdle muscular dystrophytopic1Food and Drug Administrationorganization1gene therapiestopic1Rare disease drug developmenttopic1
Recent coverage
  • HEALTHJul 31 · 08:30 UTCSTAT NEWS
    Opinion: Limb girdle muscular dystrophy patients face a maddening reality

    The author shares their experience of being diagnosed with limb girdle muscular dystrophy (LGMD) and highlights the lack of available treatments or cures. They emphasize the urgency for faster drug development due to the irreversible muscle loss caused by delays. The article notes advancements in gene therapies and FDA opportunities to modernize rare disease treatments.

targeted treatments · Dossier · The Nexus