Dossier
limb girdle muscular dystrophy
Coverage of limb girdle muscular dystrophy in the Nexus archive.
- Opinion: Limb girdle muscular dystrophy patients face a maddening reality
The author shares their experience of being diagnosed with limb girdle muscular dystrophy (LGMD) and highlights the lack of available treatments or cures. They emphasize the urgency for faster drug development due to the irreversible muscle loss caused by delays. The article notes advancements in gene therapies and FDA opportunities to modernize rare disease treatments.