HEALTHKTLA 5
Gene therapy for children with sickle cell disease approved by FDA
The FDA has approved a new gene therapy treatment for children aged 2 or older with sickle cell disease. This marks a significant advancement in managing the condition.
Related Signal
Adjacent reporting
- Groundbreaking research led in Nashville could change sickle cell treatment for children
- ‘A leap of faith’: Nashville teen makes history with gene-editing treatment for sickle cell disease
- Clinical trial shows gene editing works for β-Thalassaemia, too
- 23-year-old becomes first in state functionally cured of sickle cell disease
- STAT+: FDA approves Orca Bio’s T cell therapy for blood cancer patients