rare diseases
Coverage of rare diseases in the Nexus archive.
- Scientists’ Side Hustle? Using AI and Quantum Computing to Generate New Peptides
Researchers are using AI and quantum computing to develop new peptides for drug development targeting underserved populations and rare diseases. The project combined funding and time to demonstrate quantum computing's potential in this field.
- New effort aims to speed the development of rare-disease treatments
The Chan Zuckerberg Biohub is launching a new funding initiative to accelerate rare-disease treatments by supporting patient-led organizations and scientists. The effort aims to build research networks, collect data, establish registries, and foster collaboration between patients, physicians, and researchers to overcome challenges in developing therapies for overlooked conditions.
- Chan Zuckerberg Initiative's Biohub to open new rare disease funding round
Chan Zuckerberg Initiative's Biohub will launch a new funding round for rare diseases and expand its AI-driven drug repurposing collaboration with Every Cure.
- ORDI honours rare disease champions at Rare Star Awards 2026
ORDI honored rare disease champions at the Rare Star Awards 2026. The event recognized individuals and organizations contributing to rare disease research and advocacy.
- Chinese scientists use supercomputer to cut new drug screening time from years to seconds
Chinese scientists have developed an AI platform called GalaxyVS that uses a supercomputer to screen chemical compounds for drug discovery, reducing the initial screening phase from years to seconds. The system aims to accelerate research for treating tumors, neurodegenerative conditions, rare diseases, and emerging infectious diseases, particularly during public health crises.
- Rare disease families find roadmap to drug development at bootcamps
Ultragenyx's Rare Bootcamp provides a roadmap for families to drive research and develop new treatments for rare diseases. The bootcamp aims to help families navigate the process of developing new treatments. This initiative brings hope to families affected by rare diseases.